Prof. Dr. med. Benedikt Schoser - Chair
Professor Benedikt Schoser is a trained neurologist, neurophysiologist, neurointensivist, palliative medicine physician and muscle pathologist. He is a professor of neurology, senior consultant neurologist and co-chair of the Friedrich-Baur-Institute, Dep. of Neurology, Ludwig-Maximilians-Universität Munich, Germany. He chairs our International Scientific Advisory Board.
Dr. Maria Ester Bernardo MD
Maria Ester Bernardo is a pediatrician and physician-scientist working in the field of HSCT and HSC gene therapy with a focus on both clinical activity and experimental/translational research. Maria Ester is Head of the Pediatric Transplant Unit at San Raffaele Hospital, Clinical Coordinator of the Pediatric Clinical Research Unit at the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget) and Associate Professor of Pediatrics at the San Raffaele Vita Salute University Medical School.
Prof. Dr. Andreas Hahn MD
Andreas Hahn is Professor of Pediatrics at the University Hospital Gießen, Germany, and has been Chief Physician of the Department of Pediatric Neurology since 2002. His special areas of interest are pediatric epilepsies, neuromuscular disorders, and neurometabolic diseases. He is particularly interested in research into Pompe disease and has been treating and following such patients for many years.
Prof. Dr. Toni Cathomen
Toni Cathomen is Professor of Cell and Gene Therapy at the University of Freiburg, Germany, and Director of the Institute for Transfusion Medicine and Gene Therapy at the University Medical Center. His research focuses on improving the efficacy and safety of designer nucleases (CRISPRCas and TALEN) for therapeutic genome editing with the aim of developing novel immune cell therapies (CAR-T cells) and hematopoietic stem cell formulations to treat patients suffering from HIV infection, primary immunodeficiencies and certain types of cancer.
Dr. Eugenio Montini
Eugenio Montini is a permanent Group Leader of a Research Unit and Head of the Vector Integration Core at SR-Tiget. Eugenio Montini's research focuses on the risks associated with the use of gene therapy vectors and develops novel therapeutic vectors with a superior biosafety profile; they also monitor the efficacy, safety and molecular dynamics of blood production in patients transplanted with genetically modified stem cells using viral vectors.